Skip to main content
NIH Record - 75th Anniversary - National Institutes of Health

Aug. 20-21

NCATS, FDA To Host Gene Therapy Workshop

Abstract representation of DNA

NCATS and FDA hold 2-day gene therapy workshop.

NCATS and the Food and Drug Administration’s Center for Biologics Evaluation and Research will host a 2-day gene therapy workshop Aug. 20-21. This event, “The Growing Promise of Gene Therapy Approaches to Rare Diseases,” will take place in Masur Auditorium, Bldg. 10.

Participants will review the state of current gene therapy approaches, identify challenges and strategies to overcome them and discuss how to collaboratively scale and accelerate gene therapy development. Proposed panel sessions will cover pre-clinical development, clinical innovation, manufacturing, partnerships and transitions, business models and patient access and gene therapy as a precision medicine tool. The ultimate goal of advancing gene therapies is to benefit patients with rare diseases.

Visit to learn more and to register. There is no admission fee to attend and the workshop also will be videocast at

Back to Top